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Webinar

How to bring a gene therapy to clinical trials: A case study of a platelet-targeted gene therapy for severe Hemophilia A

In this webinar, we delve into the work behind the study published by Professor Wilcox in NEJM.

Hear how he and his team successfully brought their platelet-targeted gene therapy for severe Hemophilia A to phase 1 trials. He discusses how they overcame key challenges and optimized the manufacturing process.

  • The science behind their exciting platelet-targeted gene therapy
  • Initial clinical outcomes for the first treated patients
  • Key challenges and how the team overcame them to bring the therapy to phase 1 trials
  • Best practices for developing gene therapy manufacturing processes
  • The crucial role of the LentiBOOST™ transduction enhancer technology in the therapy’s success.

LentiBOOST GMP Grade technology: Not for diagnostic use. Other applications must be authorized by a license from Revvity.

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